Launching any new rare diseases product can be challenging and several different strategies will need to be executed efficiently and sensitively to ensure overall success.
Our proven track record is our greatest strength, we can adapt our broad skill set and experience to meet the needs of the project, allowing us to develop deeper, richer insights which help to guide effective strategic decision making.
Through a blend of classical and novel research techniques we can ensure we target the right patients, with sensitivity and care needed to ensure the project is a success.
Examples of our recent rare diseases work include:
- Enteric Hyperoxaluria
- SAH Acute sensorineural hearing loss
- B-cell chronic lymphocytic leukaemia
- Carcinoid Syndrome
- Congenital Factor XIII deficiency
- Diffuse large B-cell lymphoma
- Duchenne Muscular Dystrophy
- Fabry disease
- Follicular lymphoma
- Fragile X syndrome
- Gaucher Disease